Lysosomal Storage Disorders: Molecular Basis and Therapeutic Approaches
| Lysosomal Storage Disorders: Molecular Basis and Therapeutic Approaches |
| Autore | Moro Enrico |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (301 p.) |
| Soggetto topico | Medicine |
| Soggetto non controllato |
A4GALT
alpha-galactosidase A animal models astrogliosis autophagy axon guidance biomarkers bone involvement cathepsin D chloroquine clathrin Dkk1 dried blood spot endocytic pathways endocytosis enzyme replacement therapy exosomes experimental therapies Fabry disease GAA biomarker Gaucher disease Gaucher Disease gene therapy GLA gene globotriaosyl-sphingosine (lysoGb3) globotriaosylceramide (Gb3) globotriaosylsphingosine glycogen hematopoietic stem cell transplantations Hurler syndrome IGF2R/M6P iPSC Krabbe disease lyso-Gb3 lysosomal diseases lysosomal storage disorder lysosomal storage disorders lysosomal targeting lysosomal α-glucosidase lysosome lysosomes MIP-1β mucolipidosis II mucopolysaccharidosis IIIB mucopolysaccharidosis type I muscle NAGLU neurodegenerative disease neuronal circuit neuronopathy newborn screening Osteoimmunology Osteopontin Parkinson disease pharmacological chaperone therapy pharmacological chaperones Pompe disease precision medicine psychosine quantitative proteomics RANK/RANKL rhGAA satellite cells second tier test sortilin substrate reduction therapy tandem mass spectrometry TGF-beta Twitcher mouse variant interpretation viral vectors visual cortex visual system Wnt/β-catenin Wnt3a α-galactosidase A |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | Lysosomal Storage Disorders |
| Record Nr. | UNINA-9910557545503321 |
Moro Enrico
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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Neuroanatomy for the XXIst Century
| Neuroanatomy for the XXIst Century |
| Autore | Kathleen S. Rockland |
| Pubbl/distr/stampa | Frontiers Media SA, 2016 |
| Descrizione fisica | 1 online resource (199 p.) |
| Collana | Frontiers Research Topics |
| Soggetto topico | Neurosciences |
| Soggetto non controllato |
FIB/SEM
fMOST Human neuroanatomy light-sheet imaging Polarized light microscopy synaptic weights text-mining two-photon tomography viral vectors |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910220050003321 |
Kathleen S. Rockland
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| Frontiers Media SA, 2016 | ||
| Lo trovi qui: Univ. Federico II | ||
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Novel Treatment Strategies for Glioblastoma
| Novel Treatment Strategies for Glioblastoma |
| Autore | Stylli Stanley |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (268 p.) |
| Soggetto topico | Medicine |
| Soggetto non controllato |
angiopoietin (Ang)
anti-angiogenesis anticancer brain cancer brain tumor cancer stem cell cancer stem cell niche cancer stem cells cell cycle chimeric antigen receptor (CAR) T cells CK2 CRISPR/Cas9 CX-4945 de novo purine synthesis differentiation drug repurposing drug targets drug-inducible gene expression endothelial nitric oxide synthase (eNOS) GBM gene therapy glioblastoma glioblastoma (GB) glioblastoma multiforme glioma immune checkpoint inhibitors immunotherapy invadopodia invasion ion channels Mardepodect metabolic reprogramming metabolic treatment migration n/a nanomedicine nerve/glial antigen 2 new trial design newly diagnosed glioblastoma NG2 novel therapy one-carbon metabolism organoids P-bi-TAT P-m-TAT PEG personalized treatment pluripotent stem cells proliferation prolyl-oligopeptidase (POP) radiotherapy RAS recurrent glioblastoma Regorafenib renin-angiotensin system SRGAP2 stem cell targeted therapy temozolomide tetrac thyrointegrin αvβ3 TP53 transforming growth factor-β (TGF-β) triazole tetrac tumor antigens tumor microenvironment vaccine vascular endothelial growth factor (VEGF) viral vectors |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557363703321 |
Stylli Stanley
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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Plant Virus Emergence
| Plant Virus Emergence |
| Autore | Goodin Michael |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (174 p.) |
| Soggetto topico | Research & information: general |
| Soggetto non controllato |
Aphis gossypii
Bemisia tabaci biopharming Bunyavirale common bean cophylogeny COVID-19 crop failure crop losses Cucumis melo cucurbit viruses cytorhabdovirus developing countries disease disease progress curve domestication centers emerging disease emerging virus epidemics epidemiology food insecurity global hallmark genes helper virus indigenous viruses infectious clone insect trapping introduced crops logistic model n/a necrovirus new encounter Nicotiana benthamiana pandemics Phaseolus vulgaris phylogeny plant diseases plant pathology plant virus plant viruses plant-based biologics production plant-virus interaction Potyviruses prevalence rhizomania RNA virus RNAseq sGFP Spearman correlation spillover sub-Saharan Africa sugar beet temporal dynamics threat tomato torrado virus ToTV vaccines vector viral vectors virus virus evolution virus host interactions virus resistance virus spread virus transmission viruses whitefly whole genome sequencing whole-genome sequencing |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557563403321 |
Goodin Michael
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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The Application of Viruses to Biotechnology
| The Application of Viruses to Biotechnology |
| Autore | Varanda Carla |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (296 p.) |
| Soggetto topico | Technology: general issues |
| Soggetto non controllato |
AAV
adeno-associated virus adeno-associated virus (AAV) vector apple latent spherical virus vector aspect ratio bacmid Bacteriophage baculovirus biocontrol bioreactor breeding of grapevine cancer cancer gene therapy cancers carotenoid biosynthesis chemokines chikungunya virus circular RNA clodronate codon harmonization codon optimization comparative genomics COVID-19 COVID-19 vaccines CPMV CRISPR CRISPR-cas9 CRISPR/Cas systems CRISPR/Cas9 diagnosis DNA-based vaccines enhancer Escherichia coli expression vectors geminivirus gene editing gene expression gene therapy genome editing genome stability grapevine heterologous expression hydrothermal vent Hypnocyclicus thermotrophus immunization infectious bursal disease virus infectious diseases insect cells jaagsiekte sheep retrovirus (JSRV) LTR lytic cassette macrophage nanotechnology Newcastle disease virus phage diversity phages pig plant genome engineering plant virus porcine epidemic diarrhea virus prevention prophage protein expression PVX recombinant Lactococcus lactis reduced generation time reverse genetics RNA-based vaccines Salmonella SARS-CoV-2 self-replicating RNA vectors theranostics TMV Tn7 transduction treatment vaccine vaccines variant strain viral resistance viral vaccines viral vector viral vectors viroid virus elimination virus-induced flowering virus-induced gene silencing (VIGS) viruses VLP VLPs VNPs |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557363903321 |
Varanda Carla
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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