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Molecular Therapies for Inherited Retinal Diseases
Molecular Therapies for Inherited Retinal Diseases
Autore Collin Rob W.J
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Descrizione fisica 1 online resource (262 p.)
Soggetto topico Biology, life sciences
Research & information: general
Soggetto non controllato AAV
ABCA4
adeno-associated viral
adeno-associated virus (AAV)
allele-specific knockdown
antisense oligonucleotides
AON-mediated exon skipping
apical polarity
apoptosis
ARPE-19 cells
autophagy
autosomal dominant
bipolar cells
CEP290
chaperones
chaperonins
choroideremia
Cilia elongation
clathrin-coated vesicles
clinical trials
clustered regularly interspaced short palindromic repeats (CRISPR)
compound therapies
cones
crumbs complex
cyclic GMP
DNA therapies
DNA-wrapped gold nanoparticles
drug delivery systems
dual AAV
endosomal trafficking
Enhanced S-Cone Syndrome (ESCS)
fetal retina
Flanders founder c.4723A >
G56R
gapmer antisense oligonucleotides
gene augmentation
gene therapy
gold nanoparticles
heat shock response
homology-directed repair (HDR)
induced pluripotent stem cell (iPSC)
inherited retinal disease
inherited retinal diseases
iPSC-derived photoreceptor precursor cells
IRD
Leber congenital amaurosis
Leber congenital amaurosis and allied retinal ciliopathies
microRNA
Müller glia
n/a
necrosis
nonprofit
NR2E3
PAR complex
patient registry
photoreceptors
protein degradation
protein folding
protein trafficking
putative dominant negative effect
REP1
retina
retinal degeneration
retinal inherited disorders
retinal organoids
retinal pigment epithelium
retinitis pigmentosa
Retinitis Pigmentosa (RP)
Retinitis Pigmentosa GTPase Regulator
retinogenesis
RNA therapies
RNA therapy
rods
RPE65
splicing modulation
spontaneous nonsense correction
Stargardt disease
T nonsense mutation
therapy
translational
translational medicine
treatment
unfolded protein response
Usher syndrome
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910674051103321
Collin Rob W.J  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
New Trends in Lyotropic Liquid Crystals
New Trends in Lyotropic Liquid Crystals
Autore Dierking Ingo
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Descrizione fisica 1 online resource (252 p.)
Soggetto topico Research and information: general
Soggetto non controllato amphiphilic
application
biaxial nematic phase
biaxial nematic transition
bragg reflection
cellulose nanocrystals
chiral nematic
chirality
cholesteric liquid crystals
chromonic
chromonics
coffee-ring effect
colloid
colloidal
colloidal suspensions
curved surface
diluted nematic systems
ferroelectricity
field behavior
gelation
glass formation
graphene oxide
hydration forces
hydrogen bonds
hydroxypropyl cellulose
kinetic arrest
liquid crystal
lyotropic
lyotropic liquid crystal
lyotropic liquid crystals
Lyotropic liquid crystals
mesogen
micelle
nanomaterial
nematic
phase behavior
physico-chemical properties
Potts
rods
SmC* phase
stabilization of nematic phases
structure
surfactants
uniaxial nematic phase
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557380303321
Dierking Ingo  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui