Bayesian Design in Clinical Trials
| Bayesian Design in Clinical Trials |
| Autore | Berchialla Paola |
| Pubbl/distr/stampa | Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022 |
| Descrizione fisica | 1 online resource (190 p.) |
| Soggetto topico |
Humanities
Social interaction |
| Soggetto non controllato |
adaptive designs
adaptive randomization Bayesian Bayesian designs bayesian inference Bayesian inference bayesian meta-analysis Bayesian monitoring Bayesian trial Bayesian trial design binary data bridging studies causal inference cisplatin clinical trial clinical trials clustering combination study distribution distance dose escalation dose-escalation dose-finding dose-response doubly robust estimation doxorubicin early phase dose finding frequentist validation futility rules highest posterior density intervals interaction interim analysis latent dirichlet allocation meta-analysis modelling assumption normal approximation oncology optimal dose combination oxaliplatin peritoneal carcinomatosis phase I PIPAC poor accrual posterior and predictive probabilities power-prior predictive analysis predictive power prior distribution prior elicitation priors propensity score randomized controlled trial rare disease sample size sample size determination stopping boundaries target allocation treatment combinations |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557608103321 |
Berchialla Paola
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| Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022 | ||
| Lo trovi qui: Univ. Federico II | ||
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Hereditary Hemorrhagic Telangiectasia : Recent Advances and Future Challenges
| Hereditary Hemorrhagic Telangiectasia : Recent Advances and Future Challenges |
| Autore | Mager Hans-Jurgen |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (228 p.) |
| Soggetto topico | Research and information: general |
| Soggetto non controllato |
activin receptor-like kinase 1 (ALK1)
activin-receptor-like kinase 1 ACVRL1 ALK1 angiogenesis antiangiogenic properties anticoagulants antiplatelets antithrombotic therapy arteriovenous malformation arteriovenous malformation (AVM) arteriovenous malformations (AVMs) AVM bazedoxifene bevacizumab biomarker biomarkers bleeding bone morphogenetic protein (BMP) catheter based embolization therapy cell adhesion cerebral ischemic lesions contrast enhanced magnetic resonance angiography endoglin Endoglin endothelial cells ENG epistaxis epistaxis severity score etamsylate FK506 gastrointestinal bleeding genetic disease genotype-phenotype correlation guidelines hereditary hemorrhagic hereditary hemorrhagic telangiectasia Hereditary hemorrhagic telangiectasia Hereditary Hemorrhagic Telangiectasia hereditary hemorrhagic telangiectasia (HHT) hereditary hemorrhagic telangiectasia (HHT), second-hit hereditary hemorrhagic telangiectasia/HHT/osler's disease HHT inflammation life expectancy liver long non-coding RNAs mechanical damage microRNA microRNAs MRI N-acetylcysteine nasal endoscopy nasal ointment non-coding RNAs nosebleeds Osler-Weber-Rendu pediatrics plasma propranolol propranolol gel pulmonary arteriovenous malformation pulmonary arteriovenous malformations raloxifene rare disease rare diseases safety screening shear stress Smad pathway Smad4 SMAD4 somatic mutation sun-induced trauma survival tacrolimus telangiectases telangiectasia telangiectasis tranexamic acid transcatheter embolotherapy transforming growth factor beta (TGF-β) transforming growth factor-beta (TGF-β) ultrasound vascular endothelial growth factor (VEGF) vascular injury vascular malformations |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | Hereditary Hemorrhagic Telangiectasia |
| Record Nr. | UNINA-9910557578003321 |
Mager Hans-Jurgen
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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Molecular Basis of Inherited Diseases in Companion Animals
| Molecular Basis of Inherited Diseases in Companion Animals |
| Autore | Bannasch Danika |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (232 p.) |
| Soggetto topico |
Biology, life sciences
Research and information: general |
| Soggetto non controllato |
4-hydroxybutyric acid
acantholysis ALDH5A1 animal model Bardet-Biedl syndrome (BBS) BBS8 BMP12 brain malformation Burmese cats Caffey disease calcium calvarial hyperostotic syndrome canine Canis familiaris Canis lupus familiaris cats CHILD syndrome ciliopathy CLE COL1A1 companion animals comparative genomics contactin craniomandibular osteopathy dermatology desmosome diabetes mellitus dog dogs Duchenne dystrophinopathy encephalopathy epidermal nevus feline Felis catus GABA genetic markers genetics genodermatosis genome-wide association study genomics GWAS horses ILVEN immunohistochemistry immunology inborn error of metabolism infantile cortical hyperostosis inherited keratinocyte Labrador retriever laminin Leonberger LIPH mendelian traits metabolic disease mitochondrion n/a neurodevelopment neurological disorder neurometabolic disorder obesity phosphoenolpyruvate-carboxykinase precision medicine primary cilia progressive retinal atrophy (PRA) rare disease retinitis pigmentosa Saint Bernard SAM syndrome single-nucleotide polymorphism skin SLC35D1 SLC37A2 SLE SSADHD succinic semialdehyde susceptibility syndecan binding protein syntenin-1 systemic lupus erythematosus TLR7 toll-like receptor veterinary medicine wgs whole genome sequence whole genome sequencing whole-genome sequence whole-genome sequencing |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557141403321 |
Bannasch Danika
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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Psychosocial Considerations for Children and Adolescents Living with Rare Diseases
| Psychosocial Considerations for Children and Adolescents Living with Rare Diseases |
| Autore | Wiener Lori |
| Pubbl/distr/stampa | MDPI - Multidisciplinary Digital Publishing Institute, 2022 |
| Descrizione fisica | 1 online resource (204 p.) |
| Soggetto topico | Psychology |
| Soggetto non controllato |
adaptation
adolescents adolescents and young adults advance care planning advocacy age-appropriate AYA transition Beckwith-Wiedemann syndrome bereavement cancer care coordination caregiving childhood cancer children chronic illness cognitive functions communication compassionate communities complex chronic conditions decision-making development E-IMD emotional-behavioral problems emotions end-of-life care equity families family burden family caregiver family caregivers gender differences genetic or rare diseases health outcomes healthcare needs illness perception inherited metabolic diseases interventions life-limiting conditions medical complexity medullary thyroid carcinoma n/a neoplasm oncology palliative care parental need parenting stress parents pediatric pediatric chronic illness pediatric to adult transition pediatrics policy preschool-age children psychological psychomotor development psychosocial psychosocial care psychosocial difficulties psychosocial distress psychosocial support public health approach rare disease rare diseases sibling siblings social adjustment social support special needs transition readiness urea cycle disorders young adults |
| ISBN | 3-0365-5090-9 |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910619466903321 |
Wiener Lori
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| MDPI - Multidisciplinary Digital Publishing Institute, 2022 | ||
| Lo trovi qui: Univ. Federico II | ||
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