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Bayesian Design in Clinical Trials
Bayesian Design in Clinical Trials
Autore Berchialla Paola
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 online resource (190 p.)
Soggetto topico Humanities
Social interaction
Soggetto non controllato adaptive designs
adaptive randomization
Bayesian
Bayesian designs
bayesian inference
Bayesian inference
bayesian meta-analysis
Bayesian monitoring
Bayesian trial
Bayesian trial design
binary data
bridging studies
causal inference
cisplatin
clinical trial
clinical trials
clustering
combination study
distribution distance
dose escalation
dose-escalation
dose-finding
dose-response
doubly robust estimation
doxorubicin
early phase dose finding
frequentist validation
futility rules
highest posterior density intervals
interaction
interim analysis
latent dirichlet allocation
meta-analysis
modelling assumption
normal approximation
oncology
optimal dose combination
oxaliplatin
peritoneal carcinomatosis
phase I
PIPAC
poor accrual
posterior and predictive probabilities
power-prior
predictive analysis
predictive power
prior distribution
prior elicitation
priors
propensity score
randomized controlled trial
rare disease
sample size
sample size determination
stopping boundaries
target allocation
treatment combinations
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557608103321
Berchialla Paola  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Hereditary Hemorrhagic Telangiectasia : Recent Advances and Future Challenges
Hereditary Hemorrhagic Telangiectasia : Recent Advances and Future Challenges
Autore Mager Hans-Jurgen
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 online resource (228 p.)
Soggetto topico Research and information: general
Soggetto non controllato activin receptor-like kinase 1 (ALK1)
activin-receptor-like kinase 1
ACVRL1
ALK1
angiogenesis
antiangiogenic properties
anticoagulants
antiplatelets
antithrombotic therapy
arteriovenous malformation
arteriovenous malformation (AVM)
arteriovenous malformations (AVMs)
AVM
bazedoxifene
bevacizumab
biomarker
biomarkers
bleeding
bone morphogenetic protein (BMP)
catheter based embolization therapy
cell adhesion
cerebral ischemic lesions
contrast enhanced magnetic resonance angiography
endoglin
Endoglin
endothelial cells
ENG
epistaxis
epistaxis severity score
etamsylate
FK506
gastrointestinal bleeding
genetic disease
genotype-phenotype correlation
guidelines
hereditary hemorrhagic
hereditary hemorrhagic telangiectasia
Hereditary hemorrhagic telangiectasia
Hereditary Hemorrhagic Telangiectasia
hereditary hemorrhagic telangiectasia (HHT)
hereditary hemorrhagic telangiectasia (HHT), second-hit
hereditary hemorrhagic telangiectasia/HHT/osler's disease
HHT
inflammation
life expectancy
liver
long non-coding RNAs
mechanical damage
microRNA
microRNAs
MRI
N-acetylcysteine
nasal endoscopy
nasal ointment
non-coding RNAs
nosebleeds
Osler-Weber-Rendu
pediatrics
plasma
propranolol
propranolol gel
pulmonary arteriovenous malformation
pulmonary arteriovenous malformations
raloxifene
rare disease
rare diseases
safety
screening
shear stress
Smad pathway
Smad4
SMAD4
somatic mutation
sun-induced trauma
survival
tacrolimus
telangiectases
telangiectasia
telangiectasis
tranexamic acid
transcatheter embolotherapy
transforming growth factor beta (TGF-β)
transforming growth factor-beta (TGF-β)
ultrasound
vascular endothelial growth factor (VEGF)
vascular injury
vascular malformations
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Altri titoli varianti Hereditary Hemorrhagic Telangiectasia
Record Nr. UNINA-9910557578003321
Mager Hans-Jurgen  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Molecular Basis of Inherited Diseases in Companion Animals
Molecular Basis of Inherited Diseases in Companion Animals
Autore Bannasch Danika
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 online resource (232 p.)
Soggetto topico Biology, life sciences
Research and information: general
Soggetto non controllato 4-hydroxybutyric acid
acantholysis
ALDH5A1
animal model
Bardet-Biedl syndrome (BBS)
BBS8
BMP12
brain malformation
Burmese cats
Caffey disease
calcium
calvarial hyperostotic syndrome
canine
Canis familiaris
Canis lupus familiaris
cats
CHILD syndrome
ciliopathy
CLE
COL1A1
companion animals
comparative genomics
contactin
craniomandibular osteopathy
dermatology
desmosome
diabetes mellitus
dog
dogs
Duchenne
dystrophinopathy
encephalopathy
epidermal nevus
feline
Felis catus
GABA
genetic markers
genetics
genodermatosis
genome-wide association study
genomics
GWAS
horses
ILVEN
immunohistochemistry
immunology
inborn error of metabolism
infantile cortical hyperostosis
inherited
keratinocyte
Labrador retriever
laminin
Leonberger
LIPH
mendelian traits
metabolic disease
mitochondrion
n/a
neurodevelopment
neurological disorder
neurometabolic disorder
obesity
phosphoenolpyruvate-carboxykinase
precision medicine
primary cilia
progressive retinal atrophy (PRA)
rare disease
retinitis pigmentosa
Saint Bernard
SAM syndrome
single-nucleotide polymorphism
skin
SLC35D1
SLC37A2
SLE
SSADHD
succinic semialdehyde
susceptibility
syndecan binding protein
syntenin-1
systemic lupus erythematosus
TLR7
toll-like receptor
veterinary medicine
wgs
whole genome sequence
whole genome sequencing
whole-genome sequence
whole-genome sequencing
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557141403321
Bannasch Danika  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Psychosocial Considerations for Children and Adolescents Living with Rare Diseases
Psychosocial Considerations for Children and Adolescents Living with Rare Diseases
Autore Wiener Lori
Pubbl/distr/stampa MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 online resource (204 p.)
Soggetto topico Psychology
Soggetto non controllato adaptation
adolescents
adolescents and young adults
advance care planning
advocacy
age-appropriate
AYA transition
Beckwith-Wiedemann syndrome
bereavement
cancer
care coordination
caregiving
childhood cancer
children
chronic illness
cognitive functions
communication
compassionate communities
complex chronic conditions
decision-making
development
E-IMD
emotional-behavioral problems
emotions
end-of-life care
equity
families
family burden
family caregiver
family caregivers
gender differences
genetic or rare diseases
health outcomes
healthcare needs
illness perception
inherited metabolic diseases
interventions
life-limiting conditions
medical complexity
medullary thyroid carcinoma
n/a
neoplasm
oncology
palliative care
parental need
parenting stress
parents
pediatric
pediatric chronic illness
pediatric to adult transition
pediatrics
policy
preschool-age children
psychological
psychomotor development
psychosocial
psychosocial care
psychosocial difficulties
psychosocial distress
psychosocial support
public health approach
rare disease
rare diseases
sibling
siblings
social adjustment
social support
special needs
transition readiness
urea cycle disorders
young adults
ISBN 3-0365-5090-9
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910619466903321
Wiener Lori  
MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui