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ABC Transporters in Human Diseases
ABC Transporters in Human Diseases
Autore Falguières Thomas
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 electronic resource (494 p.)
Soggetto topico Research & information: general
Biology, life sciences
Soggetto non controllato ABC transporters
drug action
regulatory extension
regulatory insertion
mechanism of action
MRP1
MRP4
breast cancer
proliferation
migration
invasion
cAMP
ABCG2
ABCB1
blood-brain barrier
PET
Alzheimer's disease
beta-amyloid
tariquidar
erlotinib
ABCG5
ABCG8
ATP-binding cassette transporter
cholesterol
polar relay
sitosterolemia
5' untranslated region
cis-acting elements
ABCA subfamily
bioinformatics
ABC transporter
therapy response
disease-free survival
next-generation sequencing
competitive allele-specific PCR
P-glycoprotein
amyloid-beta
neuron
SK-N-SH
gene therapy
AAV
PFIC
BSEP
ABCB11
bile salts
intrahepatic cholestasis
chaperones
PFIC2
BRIC
ATP-binding cassette transporter A1 (ABCA1)
cholesterol homeostasis
reverse cholesterol transport
HDL-C
dyslipidemia
type 2 diabetes
microparticles
ABCG2 genotype
clinico-genetic analysis
ethnic specificity
genetic variations
precision medicine
rare variant
Roma
serum uric acid
SUA-lowering therapy
urate transporter
bile secretion
ABCB4
ABCC2
ABCG5/G8
molecular partners
phytosterol
xenosterol
atherosclerosis
gall stone
ABC
transporter
ABC (ATP-binding cassette) transporters
multidrug resistance
transport
trafficking
urate
mutations
polymorphisms
ABCC6
TNAP
NT5E
Pseudoxanthoma elasticum (PXE)
cancer
membrane protein
functional divergence
calcification
pseudoxanthoma elasticum
generalized arterial calcification of infancy
pyrophosphate
therapies
ABCA7
phagocytosis
Aβ peptides
yeast
multidrug transporter
anticancer
antifungal resistance
mechanism
peroxisome
adrenoleukodystrophy
fatty acids
gout
early-onset gout
hyperuricemia
uric acid
BCRP
single nucleotide polymorphism
SNP
homology modeling
substrate-binding site
cellular ATP efflux
mutagenesis
intracellular traffic
MDR3
phosphatidylcholine
RAB GTPase
taxol
drug transport
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910674029103321
Falguières Thomas  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Advanced Therapy Medicinal Products for Eye Diseases: Goals and Challenges
Advanced Therapy Medicinal Products for Eye Diseases: Goals and Challenges
Autore Diebold Yolanda
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 electronic resource (207 p.)
Soggetto topico Medicine
Soggetto non controllato MPC polymer
dry eye
ocular surface
lacrimal fluid
mucin
3D bioprinting
cornea
retina
ophthalmology
tissue regeneration
electrospinning
conjunctiva
decellularized tissue matrix
small intestinal submucosa
urinary bladder matrix
polycaprolactone
fiber
tissue engineering
stratification
conjunctival epithelial cells
hydrogel
keratoplasty
scaffold
collagen
advanced therapy medicinal product
ATMP
cell therapy
gene therapy
eye
ocular
regulatory
marketing authorization
double-crosslinking
carbodiimide
glutaraldehyde
sodium metabisulfite
sodium borohydride
EDC/NHS
stem cells
retinal diseases
optic nerve diseases
cell replacement
cell sources
advanced therapies
ocular mucosa
blindness
CLET
limbal niche
limbal stem cell
LSCD
mesenchymal stem cell transplantation
MSCT
corneal limbus
decellularized xenograft
recellularization
mesenchymal stem cells
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Altri titoli varianti Advanced Therapy Medicinal Products for Eye Diseases
Record Nr. UNINA-9910557675503321
Diebold Yolanda  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Advances in Parvovirus Research 2020
Advances in Parvovirus Research 2020
Autore Gallinella Giorgio
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 electronic resource (258 p.)
Soggetto topico Public health & preventive medicine
Soggetto non controllato feline parvovirus
virus-like particles
VP2 protein
antibodies
AAV
neuro-degenerative disease
gene therapy
antigenicity
sequencing
virus
canine parvovirus
peri-urban
wild dogs
disease transmission
Australia
parvovirus B19
G-quadruplex
bioinformatics
antivirals
BRACO-19
pyridostatin
oncolytic viruses
rodent protoparvovirus H-1PV
virus entry
clathrin-mediated endocytosis
parvovirus
minute virus of mice
RNA processing
gene expression
canine
COVID-19
veterinary epidemiology
B19V
VP1u
receptor
PLA2
erythroid cells
biomarker
drug delivery
nanocarrier
B19 parvovirus
detection
cell cycle
permissivity
serotype
capsid
cryo-EM
genome packaging
gene delivery
bocavirus
Caribbean region
new CPV-2a
outbreak
endemic
nearly complete genomes
virus evolution
parvoviruses
nucleus
imaging of viral interactions and dynamics
analysis of protein–protein interactions
analysis of virus–chromatin interactions
AMDV
Aleutian disease
mink parvovirus
Aleutian mink disease virus
vaccine
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557370403321
Gallinella Giorgio  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Bioprocess Systems Engineering Applications in Pharmaceutical Manufacturing
Bioprocess Systems Engineering Applications in Pharmaceutical Manufacturing
Autore Pörtner Ralf
Pubbl/distr/stampa Basel, : MDPI Books, 2022
Descrizione fisica 1 electronic resource (226 p.)
Soggetto topico Technology: general issues
History of engineering & technology
Soggetto non controllato clonal cell population
phenotypic diversity
inoculum train
uncertainty-based
cell culture model
biopharmaceutical manufacturing
Escherichia coli
hybrid modeling
machine learning
model-assisted DoE
quality by design
upstream bioprocessing
surface plasmon resonance (SPR)
bioprocess
monitoring
biosensor
quality by design (QbD)
process analytical technology (PAT)
biotherapeutics production
vaccines production
CHO DP-12
computational fluid dynamics
bioreactor characterization
hydrodynamic gradients
process development
critical shear stress
Kolmogorov length scale
operational space
sensors
cell culture
spectroscopy
PAT
smart biomanufacturing
soft-sensor
Adeno-associated virus
transfection
PEI
continuous
gene therapy
microcarriers
bioreactor
transient expression
spheroid strength
β-cells
diabetes
shear stress-guided production
hydrodynamic stress
Gaussian processes
Bayes optimization
Pareto optimization
multi-objective
seed train
Chinese hamster ovary cells
cryopreservation
monoclonal antibodies
N−1 perfusion
process intensification
upstream processing
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910595072803321
Pörtner Ralf  
Basel, : MDPI Books, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Brain-Targeted Drug Delivery
Brain-Targeted Drug Delivery
Autore Sousa Flávia
Pubbl/distr/stampa MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 electronic resource (260 p.)
Soggetto topico Technology: general issues
Soggetto non controllato drug delivery into the brain
transendothelium based on receptor-mediated transcytosis
immunotherapy
Alzheimer's disease
anti-tau and anti-receptor bispecific monoclonal antibodies
Alzheimer's disease-relevant tau species
temporal-spatial pathological Aβ and tau distribution
interactions between Aβ and tau
tau clearance in microglia
tau clearance in neurons
liposome
nanoparticle
seizure
laser
ultrasound
naringenin
nanostructured lipid carrier
intranasal delivery
central composite rotatable design
depression
pomegranate seed oil
nasal delivery system
memory impairment
movement impairment
delivery to brain
improved memory
phospholipid oily gel
high-grade glioma
diffuse midline glioma
glioblastoma
IL-13Rα2
IL-13
immunotoxin
targeted therapy
GB-13
IL13.E13K-PE4E
receptor expression
acetaminophen
blood-brain barrier
claudin-5
CNS drug delivery
opioids
tight junction
microdialysis
cerebral open flow microperfusion
electrochemical biosensors
macromolecules
tolcapone
microparticles
nanoparticles
PLGA
Parkinson's disease
nose to brain delivery
gene therapy
polyplexes
hyaluronidase
glycol chitosan
brain cancer
chemoattractant
CXCL
CXCR
glioblastoma multiforme
3D cell culture systems
non-human primate
convection-enhanced delivery
neurosurgery
optogenetics
brain targeted therapy
drug delivery
cerebrospinal fluid microcirculation
brain biodistribution
ISBN 3-0365-5281-2
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910619467203321
Sousa Flávia  
MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Cellular and Molecular Mechanisms of Nephropathic Cystinosis
Cellular and Molecular Mechanisms of Nephropathic Cystinosis
Autore Levtchenko Elena N
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 electronic resource (230 p.)
Soggetto topico Medicine
Pharmacology
Soggetto non controllato cystinosis
cysteamine
bone
osteoclast
genotype
CD34+ hematopoietic stem and progenitor cells
gene therapy
pre-clinical studies
investigational new drug application
clinical trial
disulfiram
mice
zebrafish
fertility
azoospermia
hypogonadism
histopathology
mouse model
lysosomal storage disease
cell and animal models
infantile nephropathic cystinosis
bone-muscle wasting
fibroblast growth factor 23
osteoclasts
sclerostin
leptin
fractures
nephropathic cystinosis
hollow fiber membrane
3-dimensional models
autophagy
macrophages
inflammasome
proximal tubular cells
endocytosis
apoptosis
chitotriosidase
interleukins
galectin-3
novel therapies
endolysosome
epithelial cell differentiation
homeostasis
lysosomal storage diseases
mitochondrial distress
kidney proximal tubule
programmed cell death
central nervous system
cortical atrophy
arterial spin labelling
cystine blood level
lysosomal storage disorder
history
treatment strategies for cystinosis
newborn screening
clinical course
CTNS-pathogenic variants
newborn screening for cystinosis
kidney progenitors
cell model
biomarkers
cystine
kidney
therapeutic monitoring
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910585941103321
Levtchenko Elena N  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Characterization and Clinical Management of Dilated Cardiomyopathy
Characterization and Clinical Management of Dilated Cardiomyopathy
Autore Merlo Marco
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 electronic resource (232 p.)
Soggetto topico Medicine
Soggetto non controllato SCN5A
cardiac sodium channel
cardiac channelopathy
dilated cardiomyopathy
precision medicine
arrhythmias
atrial fibrillation
cardiomyopathy
heart failure
supraventricular arrhythmia
systolic dysfunction
tachycardiomyopathy
ventricular arrhythmia
left atrial strain
cardiac resynchronization therapy
muscular dystrophy
calcium
heart
gene therapy
phospholamban
Serca2a
mdx
oxidative stress
membrane stabilization
left ventricular noncompaction
congenital heart disease
congestive heart failure
non-ischemic cardiomyopathy
genetics
desmin
mitochondrial dysfunction
myopathy
whole exome sequencing
laminopathy
LMNA
biomarkers
troponin T
NT-proBNP
malignant ventricular arrhythmia
arrhythmic risk stratification
DNA methylation
alternative splicing
epigenetics
nonischemic dilated cardiomyopathy
cardiac magnetic resonance imaging
late gadolinium enhancement
long axis strain
left ventricle sphericity index
major adverse cardiovascular events
sex differences
left ventricular reverse remodelling
long-term outcomes
left ventricle non-compaction cardiomyopathy
cardiac magnetic resonance
titin
RNA binding motif protein 20 (RBM20)
sarcomere
diastolic dysfunction
phosphorylation
non-sense mRNA decay
mammalian target of rapamycin (mTOR) complex-1
duchenne muscular distrophy
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557595503321
Merlo Marco  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Genetics of Hearing Impairment
Genetics of Hearing Impairment
Autore del Castillo Ignacio
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 electronic resource (314 p.)
Soggetto topico Research & information: general
Biology, life sciences
Genetics (non-medical)
Soggetto non controllato inner ear
hearing impairment
gene identification
disease-causing mutations
genetic epidemiology
genotype&ndash
phenotype correlations
pathophysiological mechanisms
omics
genome editing
gene therapy
ISBN 3-0365-5224-3
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910637793003321
del Castillo Ignacio  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Lysosomal Storage Disorders: Molecular Basis and Therapeutic Approaches
Lysosomal Storage Disorders: Molecular Basis and Therapeutic Approaches
Autore Moro Enrico
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 electronic resource (301 p.)
Soggetto topico Medicine
Soggetto non controllato mucopolysaccharidosis IIIB
quantitative proteomics
NAGLU
lysosomes
Gaucher disease
bone involvement
enzyme replacement therapy
substrate reduction therapy
Osteoimmunology
RANK/RANKL
Osteopontin
MIP-1β
mucolipidosis II
sortilin
TGF-beta
cathepsin D
Fabry disease
alpha-galactosidase A
endocytosis
lysosome
IGF2R/M6P
clathrin
chloroquine
lysosomal diseases
precision medicine
pharmacological chaperones
gene therapy
Pompe disease
lysosomal targeting
autophagy
muscle
satellite cells
rhGAA
glycogen
lysosomal α-glucosidase
GAA biomarker
Gaucher Disease
Wnt/β-catenin
Dkk1
Wnt3a
iPSC
neuronopathy
Krabbe disease
Twitcher mouse
psychosine
visual system
visual cortex
astrogliosis
mucopolysaccharidosis type I
Hurler syndrome
hematopoietic stem cell transplantations
animal models
experimental therapies
axon guidance
lysosomal storage disorders
neuronal circuit
α-galactosidase A
A4GALT
globotriaosylceramide (Gb3)
globotriaosyl-sphingosine (lysoGb3)
pharmacological chaperone therapy
exosomes
endocytic pathways
neurodegenerative disease
Parkinson disease
lysosomal storage disorder
viral vectors
newborn screening
variant interpretation
second tier test
tandem mass spectrometry
lyso-Gb3
dried blood spot
GLA gene
globotriaosylsphingosine
biomarkers
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Altri titoli varianti Lysosomal Storage Disorders
Record Nr. UNINA-9910557545503321
Moro Enrico  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
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Measurement Technologies for up- and Downstream Bioprocessing
Measurement Technologies for up- and Downstream Bioprocessing
Autore Mandenius Carl-Fredrik
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Descrizione fisica 1 electronic resource (160 p.)
Soggetto topico Technology: general issues
Soggetto non controllato lactate biosensor
enzyme electrode
off-line monitoring
screen-printing
at-line measurement
in-line monitoring
cell viability
prediction
chromatogram fingerprinting
filamentous fungi
Penicillium chrysogenum
Trichoderma reesei Rut-C30
HPLC-SEC
AAV-adeno-associated virus
insect cell-baculovirus
cell culture monitoring
digital holographic microscopy
process analytical technology
pH
pCO2
off-gas measurement
carbon dioxide
cell culture
reference
CHO
automated sampling
bioprocess
amino acids
vitamins
Raman spectroscopy
mammalian cell culture
high-throughput
scale-down technologies
cation exchange chromatography
monitoring
PAT
IgG titer
real-time
on-line
nanoplasmonic
gene therapy
dielectric spectroscopy
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557333203321
Mandenius Carl-Fredrik  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021
Materiale a stampa
Lo trovi qui: Univ. Federico II
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