Molecular Basis and Gene Therapies of Cystic Fibrosis
| Molecular Basis and Gene Therapies of Cystic Fibrosis |
| Autore | Engelhardt John |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020 |
| Descrizione fisica | 1 online resource (210 p.) |
| Soggetto topico | Medicine |
| Soggetto non controllato |
airway basal cell
baculovirus biomarker CFTR CFTR gene CFTR modulators CFTR variants CFTR-related disorders common and new pathogenic variants cyclophosphamide cystic fibrosis Cystic fibrosis disease liability drug development enterotoxin gene cluster ethnic Russian population exosomes functional assay gene therapy genotype-guided therapy genotype-phenotype correlations gut-lung axis health policies health policy human nasal epithelial cells incidence insect cells interpretation lentivirus lung lung microbiome metagenomics microvesicles miRNA molecular diagnosis MRSA newborn screening next generation sequencing Next Generation Sequencing (NGS) organoids penetrance pre-clinical in vitro models primary cells proteostasis rAAV2/HBoV1 small molecules Staphylococcus aureus superantigen survival transcriptomics transient immunosuppression trypsinogen |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557392203321 |
Engelhardt John
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020 | ||
| Lo trovi qui: Univ. Federico II | ||
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The Application of Viruses to Biotechnology
| The Application of Viruses to Biotechnology |
| Autore | Varanda Carla |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 |
| Descrizione fisica | 1 online resource (296 p.) |
| Soggetto topico | Technology: general issues |
| Soggetto non controllato |
AAV
adeno-associated virus adeno-associated virus (AAV) vector apple latent spherical virus vector aspect ratio bacmid Bacteriophage baculovirus biocontrol bioreactor breeding of grapevine cancer cancer gene therapy cancers carotenoid biosynthesis chemokines chikungunya virus circular RNA clodronate codon harmonization codon optimization comparative genomics COVID-19 COVID-19 vaccines CPMV CRISPR CRISPR-cas9 CRISPR/Cas systems CRISPR/Cas9 diagnosis DNA-based vaccines enhancer Escherichia coli expression vectors geminivirus gene editing gene expression gene therapy genome editing genome stability grapevine heterologous expression hydrothermal vent Hypnocyclicus thermotrophus immunization infectious bursal disease virus infectious diseases insect cells jaagsiekte sheep retrovirus (JSRV) LTR lytic cassette macrophage nanotechnology Newcastle disease virus phage diversity phages pig plant genome engineering plant virus porcine epidemic diarrhea virus prevention prophage protein expression PVX recombinant Lactococcus lactis reduced generation time reverse genetics RNA-based vaccines Salmonella SARS-CoV-2 self-replicating RNA vectors theranostics TMV Tn7 transduction treatment vaccine vaccines variant strain viral resistance viral vaccines viral vector viral vectors viroid virus elimination virus-induced flowering virus-induced gene silencing (VIGS) viruses VLP VLPs VNPs |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557363903321 |
Varanda Carla
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2021 | ||
| Lo trovi qui: Univ. Federico II | ||
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