Molecular Therapies for Inherited Retinal Diseases
| Molecular Therapies for Inherited Retinal Diseases |
| Autore | Collin Rob W.J |
| Pubbl/distr/stampa | Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020 |
| Descrizione fisica | 1 online resource (262 p.) |
| Soggetto topico |
Biology, life sciences
Research & information: general |
| Soggetto non controllato |
AAV
ABCA4 adeno-associated viral adeno-associated virus (AAV) allele-specific knockdown antisense oligonucleotides AON-mediated exon skipping apical polarity apoptosis ARPE-19 cells autophagy autosomal dominant bipolar cells CEP290 chaperones chaperonins choroideremia Cilia elongation clathrin-coated vesicles clinical trials clustered regularly interspaced short palindromic repeats (CRISPR) compound therapies cones crumbs complex cyclic GMP DNA therapies DNA-wrapped gold nanoparticles drug delivery systems dual AAV endosomal trafficking Enhanced S-Cone Syndrome (ESCS) fetal retina Flanders founder c.4723A > G56R gapmer antisense oligonucleotides gene augmentation gene therapy gold nanoparticles heat shock response homology-directed repair (HDR) induced pluripotent stem cell (iPSC) inherited retinal disease inherited retinal diseases iPSC-derived photoreceptor precursor cells IRD Leber congenital amaurosis Leber congenital amaurosis and allied retinal ciliopathies microRNA Müller glia n/a necrosis nonprofit NR2E3 PAR complex patient registry photoreceptors protein degradation protein folding protein trafficking putative dominant negative effect REP1 retina retinal degeneration retinal inherited disorders retinal organoids retinal pigment epithelium retinitis pigmentosa Retinitis Pigmentosa (RP) Retinitis Pigmentosa GTPase Regulator retinogenesis RNA therapies RNA therapy rods RPE65 splicing modulation spontaneous nonsense correction Stargardt disease T nonsense mutation therapy translational translational medicine treatment unfolded protein response Usher syndrome |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910674051103321 |
Collin Rob W.J
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| Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020 | ||
| Lo trovi qui: Univ. Federico II | ||
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New Insights on Biofilm Antimicrobial Strategies, 2nd Volume
| New Insights on Biofilm Antimicrobial Strategies, 2nd Volume |
| Autore | Melo Luís |
| Pubbl/distr/stampa | Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022 |
| Descrizione fisica | 1 online resource (160 p.) |
| Soggetto topico |
Biology, life sciences
Microbiology (non-medical) Research & information: general |
| Soggetto non controllato |
1-O-alkyl-sn-glycerols
2'OMe aluminum nitride anti-fouling antibacterial antibacterial agents antibacterial drug antibiofilm activity antifungal antimicrobial antimicrobial activity antimicrobial resistance antisense oligonucleotides apoptosis bacteriophages benzalkonium chloride biocidal particles biocontrol biofilm biofilms Candida CAPE cellulose acetate ciprofloxacin composite dental implants displacement E. coli biofilms Escherichia coli ether lipids food contact surfaces functionalization heat shock Lactobacillus plantarum Lactobacillus rhamnosus LNA mechanical microbial resistance n/a natural alkylglycerols nucleic acid mimics oral biofilm organic matter peracetic acid polypropylene probiotics prosthesis-related infections quorum sensing inhibition stainless steel surface coating thermal titanium implants urinary tract devices vitamin B12 |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910585938403321 |
Melo Luís
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| Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022 | ||
| Lo trovi qui: Univ. Federico II | ||
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Oligonucleotide, Therapy, and Applications
| Oligonucleotide, Therapy, and Applications |
| Autore | Aliño Salvador |
| Pubbl/distr/stampa | Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022 |
| Descrizione fisica | 1 online resource (123 p.) |
| Soggetto topico | Medicine |
| Soggetto non controllato |
Amplex Red
anti-proliferative activity antisense oligonucleotide antisense oligonucleotides antisensense oligonucleotide aptamer aptasensor covalent dimer construct DNA methylation DNAzyme dopamine neurotransmission double mutant A30P*A53T* exon skipping fibrillin-1 Foxp3 G-quadruplexes histone code influenza light-induced activity Marfan syndrome microRNA motor deficits nanoparticles noncoding RNA Parkinson's disease primary cell culture of human glioma pulmonary arterial hypertension quantum dots (QDs) regulatory T cells ROS SERS splice-switching Sporothrix schenckii transgenic mouse model vaccine immunogenicity virus detection α-synuclein |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910557615903321 |
Aliño Salvador
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| Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022 | ||
| Lo trovi qui: Univ. Federico II | ||
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