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Molecular Therapies for Inherited Retinal Diseases
Molecular Therapies for Inherited Retinal Diseases
Autore Collin Rob W.J
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Descrizione fisica 1 online resource (262 p.)
Soggetto topico Biology, life sciences
Research & information: general
Soggetto non controllato AAV
ABCA4
adeno-associated viral
adeno-associated virus (AAV)
allele-specific knockdown
antisense oligonucleotides
AON-mediated exon skipping
apical polarity
apoptosis
ARPE-19 cells
autophagy
autosomal dominant
bipolar cells
CEP290
chaperones
chaperonins
choroideremia
Cilia elongation
clathrin-coated vesicles
clinical trials
clustered regularly interspaced short palindromic repeats (CRISPR)
compound therapies
cones
crumbs complex
cyclic GMP
DNA therapies
DNA-wrapped gold nanoparticles
drug delivery systems
dual AAV
endosomal trafficking
Enhanced S-Cone Syndrome (ESCS)
fetal retina
Flanders founder c.4723A >
G56R
gapmer antisense oligonucleotides
gene augmentation
gene therapy
gold nanoparticles
heat shock response
homology-directed repair (HDR)
induced pluripotent stem cell (iPSC)
inherited retinal disease
inherited retinal diseases
iPSC-derived photoreceptor precursor cells
IRD
Leber congenital amaurosis
Leber congenital amaurosis and allied retinal ciliopathies
microRNA
Müller glia
n/a
necrosis
nonprofit
NR2E3
PAR complex
patient registry
photoreceptors
protein degradation
protein folding
protein trafficking
putative dominant negative effect
REP1
retina
retinal degeneration
retinal inherited disorders
retinal organoids
retinal pigment epithelium
retinitis pigmentosa
Retinitis Pigmentosa (RP)
Retinitis Pigmentosa GTPase Regulator
retinogenesis
RNA therapies
RNA therapy
rods
RPE65
splicing modulation
spontaneous nonsense correction
Stargardt disease
T nonsense mutation
therapy
translational
translational medicine
treatment
unfolded protein response
Usher syndrome
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910674051103321
Collin Rob W.J  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
New Insights on Biofilm Antimicrobial Strategies, 2nd Volume
New Insights on Biofilm Antimicrobial Strategies, 2nd Volume
Autore Melo Luís
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 online resource (160 p.)
Soggetto topico Biology, life sciences
Microbiology (non-medical)
Research & information: general
Soggetto non controllato 1-O-alkyl-sn-glycerols
2'OMe
aluminum nitride
anti-fouling
antibacterial
antibacterial agents
antibacterial drug
antibiofilm activity
antifungal
antimicrobial
antimicrobial activity
antimicrobial resistance
antisense oligonucleotides
apoptosis
bacteriophages
benzalkonium chloride
biocidal particles
biocontrol
biofilm
biofilms
Candida
CAPE
cellulose acetate
ciprofloxacin
composite
dental implants
displacement
E. coli biofilms
Escherichia coli
ether lipids
food contact surfaces
functionalization
heat shock
Lactobacillus plantarum
Lactobacillus rhamnosus
LNA
mechanical
microbial resistance
n/a
natural alkylglycerols
nucleic acid mimics
oral biofilm
organic matter
peracetic acid
polypropylene
probiotics
prosthesis-related infections
quorum sensing inhibition
stainless steel
surface coating
thermal
titanium implants
urinary tract devices
vitamin B12
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910585938403321
Melo Luís  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Oligonucleotide, Therapy, and Applications
Oligonucleotide, Therapy, and Applications
Autore Aliño Salvador
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 online resource (123 p.)
Soggetto topico Medicine
Soggetto non controllato Amplex Red
anti-proliferative activity
antisense oligonucleotide
antisense oligonucleotides
antisensense oligonucleotide
aptamer
aptasensor
covalent dimer construct
DNA methylation
DNAzyme
dopamine neurotransmission
double mutant A30P*A53T*
exon skipping
fibrillin-1
Foxp3
G-quadruplexes
histone code
influenza
light-induced activity
Marfan syndrome
microRNA
motor deficits
nanoparticles
noncoding RNA
Parkinson's disease
primary cell culture of human glioma
pulmonary arterial hypertension
quantum dots (QDs)
regulatory T cells
ROS
SERS
splice-switching
Sporothrix schenckii
transgenic mouse model
vaccine immunogenicity
virus detection
α-synuclein
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557615903321
Aliño Salvador  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui