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Molecular Therapies for Inherited Retinal Diseases
Molecular Therapies for Inherited Retinal Diseases
Autore Collin Rob W.J
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Descrizione fisica 1 electronic resource (262 p.)
Soggetto topico Research & information: general
Biology, life sciences
Soggetto non controllato induced pluripotent stem cell (iPSC)
clustered regularly interspaced short palindromic repeats (CRISPR)
homology-directed repair (HDR)
Enhanced S-Cone Syndrome (ESCS)
NR2E3
AAV
retina
gene therapy
dual AAV
gold nanoparticles
DNA-wrapped gold nanoparticles
ARPE-19 cells
retinal pigment epithelium
clathrin-coated vesicles
endosomal trafficking
retinitis pigmentosa
autosomal dominant
G56R
putative dominant negative effect
gapmer antisense oligonucleotides
allele-specific knockdown
Leber congenital amaurosis and allied retinal ciliopathies
CEP290
Flanders founder c.4723A >
T nonsense mutation
Cilia elongation
spontaneous nonsense correction
AON-mediated exon skipping
microRNA
photoreceptors
rods
cones
bipolar cells
Müller glia
retinal inherited disorders
retinal degeneration
antisense oligonucleotides
Stargardt disease
inherited retinal diseases
splicing modulation
RNA therapy
ABCA4
iPSC-derived photoreceptor precursor cells
cyclic GMP
apoptosis
necrosis
drug delivery systems
translational medicine
Usher syndrome
Leber congenital amaurosis
RPE65
nonprofit
patient registry
translational
protein trafficking
protein folding
protein degradation
chaperones
chaperonins
heat shock response
unfolded protein response
autophagy
therapy
IRD
DNA therapies
RNA therapies
compound therapies
clinical trials
Retinitis Pigmentosa GTPase Regulator
adeno-associated viral
Retinitis Pigmentosa (RP)
choroideremia
REP1
inherited retinal disease
treatment
apical polarity
crumbs complex
fetal retina
PAR complex
retinal organoids
retinogenesis
gene augmentation
adeno-associated virus (AAV)
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910674051103321
Collin Rob W.J  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
New Insights on Biofilm Antimicrobial Strategies, 2nd Volume
New Insights on Biofilm Antimicrobial Strategies, 2nd Volume
Autore Melo Luís
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 electronic resource (160 p.)
Soggetto topico Research & information: general
Biology, life sciences
Microbiology (non-medical)
Soggetto non controllato antibacterial drug
vitamin B12
antisense oligonucleotides
nucleic acid mimics
LNA
2'OMe
biocidal particles
functionalization
benzalkonium chloride
Escherichia coli
antimicrobial activity
antimicrobial resistance
natural alkylglycerols
ether lipids
1-O-alkyl-sn-glycerols
antibiofilm activity
quorum sensing inhibition
stainless steel
polypropylene
organic matter
microbial resistance
peracetic acid
biofilms
prosthesis-related infections
heat shock
ciprofloxacin
antibacterial agents
E. coli biofilms
food contact surfaces
biocontrol
bacteriophages
aluminum nitride
composite
antibacterial
mechanical
thermal
cellulose acetate
CAPE
Candida
antifungal
biofilm
apoptosis
urinary tract devices
probiotics
Lactobacillus plantarum
Lactobacillus rhamnosus
displacement
oral biofilm
dental implants
titanium implants
antimicrobial
surface coating
anti-fouling
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910585938403321
Melo Luís  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Oligonucleotide, Therapy, and Applications
Oligonucleotide, Therapy, and Applications
Autore Aliño Salvador
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 electronic resource (123 p.)
Soggetto topico Medicine
Soggetto non controllato quantum dots (QDs)
DNAzyme
ROS
Amplex Red
light-induced activity
DNA methylation
histone code
microRNA
nanoparticles
noncoding RNA
pulmonary arterial hypertension
aptamer
aptasensor
influenza
SERS
virus detection
α-synuclein
antisense oligonucleotide
dopamine neurotransmission
double mutant A30P*A53T*
motor deficits
Parkinson’s disease
transgenic mouse model
G-quadruplexes
covalent dimer construct
anti-proliferative activity
primary cell culture of human glioma
antisensense oligonucleotide
Foxp3
regulatory T cells
vaccine immunogenicity
Sporothrix schenckii
Marfan syndrome
fibrillin-1
antisense oligonucleotides
exon skipping
splice-switching
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557615903321
Aliño Salvador  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui