top

  Info

  • Utilizzare la checkbox di selezione a fianco di ciascun documento per attivare le funzionalità di stampa, invio email, download nei formati disponibili del (i) record.

  Info

  • Utilizzare questo link per rimuovere la selezione effettuata.
Advance in the Treatment of Pediatric Leukemia
Advance in the Treatment of Pediatric Leukemia
Autore Handgretinger Rupert
Pubbl/distr/stampa Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Descrizione fisica 1 online resource (300 p.)
Soggetto topico Chemistry
Research & information: general
Soggetto non controllato 5-azacitidine
ABCC4
acute lymphoblastic leukemia
acute myeloid leukemia
acute pancreatitis
ADC
advances
ALL
allogeneic stem cell transplantation
alternative donors
AML
antibody
antibody-drug conjugate
B-ALL
BCL11B
BCP-ALL
bispecific T-cell engager (BiTE)
CD19
CFTR
childhood acute lymphoblastic leukemia
children
chronic myeloid leukemia
CML
conditioning regimen
COVID-19
diagnosis
DUX4
evolution of CAR T cells
Fc-engineering
FDA-approved CAR products
future directions of CAR T cell therapy
genome
hematopoietic stem cell transplantation
IKZF1
immunizations
immunotherapy
juvenile myelomonocytic leukemia
L-asparaginase
leukemia
limitations and complications of CAR T cell therapy
low-risk ALL
lymphoblastic leukemia
minimal residual disease
myelodysplastic/myeloproliferative disorders
n/a
NOTCH1
NUTM1
other extramedullary relapse
PAX5
pediatric
pediatric leukemia
Ph-like
polymorphism
prognosis
RAS signaling
risk-stratified treatment
SNV
T-ALL
targeted therapy
TcR versus CAR
TRAIL
transcriptome
treatment
treatment related toxicity
tyrosine kinase inhibitor
xenograft
ZNF384
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910576878903321
Handgretinger Rupert  
Basel, : MDPI - Multidisciplinary Digital Publishing Institute, 2022
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Molecular Basis and Gene Therapies of Cystic Fibrosis
Molecular Basis and Gene Therapies of Cystic Fibrosis
Autore Engelhardt John
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Descrizione fisica 1 online resource (210 p.)
Soggetto topico Medicine
Soggetto non controllato airway basal cell
baculovirus
biomarker
CFTR
CFTR gene
CFTR modulators
CFTR variants
CFTR-related disorders
common and new pathogenic variants
cyclophosphamide
cystic fibrosis
Cystic fibrosis
disease liability
drug development
enterotoxin gene cluster
ethnic Russian population
exosomes
functional assay
gene therapy
genotype-guided therapy
genotype-phenotype correlations
gut-lung axis
health policies
health policy
human nasal epithelial cells
incidence
insect cells
interpretation
lentivirus
lung
lung microbiome
metagenomics
microvesicles
miRNA
molecular diagnosis
MRSA
newborn screening
next generation sequencing
Next Generation Sequencing (NGS)
organoids
penetrance
pre-clinical in vitro models
primary cells
proteostasis
rAAV2/HBoV1
small molecules
Staphylococcus aureus
superantigen
survival
transcriptomics
transient immunosuppression
trypsinogen
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Record Nr. UNINA-9910557392203321
Engelhardt John  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui
Peptide Nucleic Acids : Applications in Biomedical Sciences
Peptide Nucleic Acids : Applications in Biomedical Sciences
Autore Yavin Eylon
Pubbl/distr/stampa Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Descrizione fisica 1 online resource (154 p.)
Soggetto topico Medicine and Nursing
Soggetto non controllato antibacterials
antisense
bacterial resistance
cancer
catalytic hairpin assembly (CHA)
CFTR
colorimetric detection
conjugates
cystic fibrosis
delivery
drug resistance
electrochemical biosensors
exon inclusion
exon skipping
fluorescence
gene editing
influenza virus
l-DNA
light-triggered
microRNA
microRNAs
miR-145-5p
miRNA targeting
n/a
nanoparticles
oligonucleotides
peptide nucleic acid
peptide nucleic acid (PNA)
peptide nucleic acids
Peptide nucleic acids
peptide nucleic acids (PNAs)
PNA
PNA transporters
PNA-masking
polymerase chain reaction (PCR)
recombination
repair
RNA
RNA structure
single nucleotide polymorphism
single-nucleotide polymorphism (SNP)
strand invasion
strand-displacement reaction
structure
templated reactions
tolane
triplex
β-thalassemia
Formato Materiale a stampa
Livello bibliografico Monografia
Lingua di pubblicazione eng
Altri titoli varianti Peptide Nucleic Acids
Record Nr. UNINA-9910557110203321
Yavin Eylon  
Basel, Switzerland, : MDPI - Multidisciplinary Digital Publishing Institute, 2020
Materiale a stampa
Lo trovi qui: Univ. Federico II
Opac: Controlla la disponibilità qui