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Expert opinion on orphan drugs
| Expert opinion on orphan drugs |
| Pubbl/distr/stampa | [London] : , : Informa Healthcare, , 2013- |
| Descrizione fisica | 1 online resource |
| Disciplina | 615 |
| Soggetto topico |
Rare diseases
Orphan drugs Chemotherapy Orphan Drug Production Rare Diseases |
| Soggetto genere / forma |
Periodical
Periodicals. |
| Formato | Materiale a stampa  |
| Livello bibliografico | Periodico |
| Lingua di pubblicazione | eng |
| Record Nr. | UNINA-9910735299003321 |
| [London] : , : Informa Healthcare, , 2013- | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
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La FDA combate las enfermedades raras [[electronic resource] ] : nueva ayuda para pacientes sin tratamientos
| La FDA combate las enfermedades raras [[electronic resource] ] : nueva ayuda para pacientes sin tratamientos |
| Edizione | [Rev. Feb. 2002.] |
| Pubbl/distr/stampa | Rockville, MD : , : Dept. of Health and Human Services, Food and Drug Administration, Office of Public Affairs, , [2002] |
| Descrizione fisica | 1 sheet : digital, PDF file |
| Collana |
Just the facts
Publication |
| Soggetto topico |
Rare diseases - Treatment
Orphan drugs |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | spa |
| Altri titoli varianti | FDA combate las enfermedades raras |
| Record Nr. | UNINA-9910695438503321 |
| Rockville, MD : , : Dept. of Health and Human Services, Food and Drug Administration, Office of Public Affairs, , [2002] | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
| ||
FDA fights rare diseases [[electronic resource] ] : new help for patients without treatments
| FDA fights rare diseases [[electronic resource] ] : new help for patients without treatments |
| Edizione | [Rev. Feb. 2002.] |
| Pubbl/distr/stampa | Rockville, MD : , : Dept. of Health and Human Services, Food and Drug Administration, Office of Public Affairs, , [2002] |
| Descrizione fisica | 1 sheet : digital, PDF file |
| Collana |
Just the facts
Publication |
| Soggetto topico |
Rare diseases - Treatment
Orphan drugs |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | FDA fights rare diseases |
| Record Nr. | UNINA-9910695574303321 |
| Rockville, MD : , : Dept. of Health and Human Services, Food and Drug Administration, Office of Public Affairs, , [2002] | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
| ||
Orphan drugs : research and reviews
| Orphan drugs : research and reviews |
| Pubbl/distr/stampa | [Auckland, N.Z.] : , : Dovepress, , 2011- |
| Disciplina | 615.1 |
| Soggetto topico | Orphan drugs |
| Soggetto genere / forma | Periodicals. |
| Formato | Materiale a stampa |
| Livello bibliografico | Periodico |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | Journal of orphan drugs : research and reviews |
| Record Nr. | UNINA-9910141529403321 |
| [Auckland, N.Z.] : , : Dovepress, , 2011- | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
| ||
Orphan drugs : research and reviews
| Orphan drugs : research and reviews |
| Pubbl/distr/stampa | [Auckland, N.Z.] : , : Dovepress, , 2011- |
| Disciplina | 615.1 |
| Soggetto topico | Orphan drugs |
| Soggetto genere / forma | Periodicals. |
| Formato | Materiale a stampa |
| Livello bibliografico | Periodico |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | Journal of orphan drugs : research and reviews |
| Record Nr. | UNISA-996321071703316 |
| [Auckland, N.Z.] : , : Dovepress, , 2011- | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. di Salerno | ||
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Providing for consideration of the bill (H.R. 1629) to amend the Federal Food, Drug, and Cosmetic Act with respect to limitations on exclusive approval or licensure of orphan drugs, and for other purposes; providing for consideration of the resolution (H. Res. 275) condemning the horrific shootings in Atlanta, Georgia, on March 16, 2021, and reaffirming the House of Representative's commitment to combating hate, bigotry, and violence against the Asian-American and Pacific Islander community; and for other purposes : report (to accompany H. Res. 403)
| Providing for consideration of the bill (H.R. 1629) to amend the Federal Food, Drug, and Cosmetic Act with respect to limitations on exclusive approval or licensure of orphan drugs, and for other purposes; providing for consideration of the resolution (H. Res. 275) condemning the horrific shootings in Atlanta, Georgia, on March 16, 2021, and reaffirming the House of Representative's commitment to combating hate, bigotry, and violence against the Asian-American and Pacific Islander community; and for other purposes : report (to accompany H. Res. 403) |
| Pubbl/distr/stampa | [Washington, D.C.] : , : [U.S. Government Publishing Office], , 2021 |
| Descrizione fisica | 1 online resource (4 pages) |
| Disciplina | 1.1/8:117-37 |
| Collana | Report / 117th Congress, 1st session, House of Representatives |
| Soggetto topico |
Orphan drugs - United States
Asian Americans - Violence against - Prevention Pacific Islander Americans - Violence against - Prevention Orphan drugs |
| Soggetto genere / forma |
Legislative materials.
Rules. |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | PROVIDING FOR CONSIDERATION OF THE BILL |
| Record Nr. | UNINA-9910717337203321 |
| [Washington, D.C.] : , : [U.S. Government Publishing Office], , 2021 | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
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Rare diseases : expediting treatments for patients : hearing before the Subcommittee on Children and Families of the Committee on Health, Education, Labor, and Pensions, United States Senate, One Hundred Fifteenth Congress, second session, on examining rare diseases, focusing on expediting treatments for patients, October 3, 2018
| Rare diseases : expediting treatments for patients : hearing before the Subcommittee on Children and Families of the Committee on Health, Education, Labor, and Pensions, United States Senate, One Hundred Fifteenth Congress, second session, on examining rare diseases, focusing on expediting treatments for patients, October 3, 2018 |
| Pubbl/distr/stampa | Washington : , : U.S. Government Publishing Office, , 2020 |
| Descrizione fisica | 1 online resource (iii, 40 pages) |
| Collana | S. hrg. |
| Soggetto topico |
Rare diseases - Treatment
Orphan drugs Drug approval |
| Soggetto genere / forma |
Legislative hearings.
Rules. |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Altri titoli varianti | Rare diseases |
| Record Nr. | UNINA-9910714098603321 |
| Washington : , : U.S. Government Publishing Office, , 2020 | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
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Rare diseases and orphan products [[electronic resource] ] : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies
| Rare diseases and orphan products [[electronic resource] ] : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies |
| Pubbl/distr/stampa | Washington, D.C., : National Academies Press, c2010 |
| Descrizione fisica | 1 online resource (443 p.) |
| Disciplina | 615.19 |
| Altri autori (Persone) |
FieldMarilyn J (Marilyn Jane)
BoatThomas F |
| Soggetto topico |
Orphan drugs
Drugs - Design Rare diseases - Treatment |
| Soggetto genere / forma | Electronic books. |
| ISBN |
1-283-04456-0
9786613044563 0-309-15807-9 |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Nota di contenuto |
""Front Matter""; ""Acknowledgments""; ""Reviewers""; ""Preface""; ""Contents""; ""Boxes, Figures, and Tables""; ""Summary""; ""1 Introduction""; ""2 Profile of Rare Diseases""; ""3 Regulatory Framework for Drugs for Rare Diseases""; ""4 Discovery Research for Rare Diseases and Orphan Product Development""; ""5 Development of New Therapeutic Drugs and Biologics for Rare Diseases""; ""6 Coverage and Reimbursement: Incentives and Disincentives for Product Development""; ""7 Medical Devices: Research and Development for Rare Diseases""
""8 Toward an Integrated Approach to Accelerating Research and Product Development for Rare Diseases""""References""; ""Appendix A: Study Activities""; ""Appendix B: Innovation and the Orphan Drug Act, 1983-2009: Regulatory and Clinical Characteristics of Approved Orphan Drugs""; ""Appendix C: Medicare Part D Coverage and Reimbursement of Orphan Drugs""; ""Appendix D: Glossary, Abbreviations, and Public Laws""; ""Appendix E: Rare Diseases Clinical Research Network""; ""Appendix F: Advocacy Group Approaches to Accelerating Research and Product Development: Illustrative Examples"" ""Appendix G: Committee and Staff Biographies""""Index"" |
| Record Nr. | UNINA-9910456868603321 |
| Washington, D.C., : National Academies Press, c2010 | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
| ||
Rare diseases and orphan products : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies
| Rare diseases and orphan products : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies |
| Pubbl/distr/stampa | Washington, D.C. : , : National Academies Press, , 2010 |
| Descrizione fisica | 1 online resource (xxi, 420 pages) : illustrations |
| Disciplina | 615.19 |
| Altri autori (Persone) |
FieldMarilyn J (Marilyn Jane)
BoatThomas F |
| Soggetto topico |
Orphan drugs
Drugs - Design Rare diseases - Treatment |
| ISBN |
0-309-20991-9
1-283-04456-0 9786613044563 0-309-15807-9 |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Nota di contenuto |
""Front Matter""; ""Acknowledgments""; ""Reviewers""; ""Preface""; ""Contents""; ""Boxes, Figures, and Tables""; ""Summary""; ""1 Introduction""; ""2 Profile of Rare Diseases""; ""3 Regulatory Framework for Drugs for Rare Diseases""; ""4 Discovery Research for Rare Diseases and Orphan Product Development""; ""5 Development of New Therapeutic Drugs and Biologics for Rare Diseases""; ""6 Coverage and Reimbursement: Incentives and Disincentives for Product Development""; ""7 Medical Devices: Research and Development for Rare Diseases""
""8 Toward an Integrated Approach to Accelerating Research and Product Development for Rare Diseases""; ""References""; ""Appendix A: Study Activities""; ""Appendix B: Innovation and the Orphan Drug Act, 1983-2009: Regulatory and Clinical Characteristics of Approved Orphan Drugs""; ""Appendix C: Medicare Part D Coverage and Reimbursement of Orphan Drugs""; ""Appendix D: Glossary, Abbreviations, and Public Laws""; ""Appendix E: Rare Diseases Clinical Research Network""; ""Appendix F: Advocacy Group Approaches to Accelerating Research and Product Development: Illustrative Examples""; ""Appendix G: Committee and Staff Biographies""; ""Index"" |
| Record Nr. | UNINA-9910781004803321 |
| Washington, D.C. : , : National Academies Press, , 2010 | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
| ||
Rare diseases and orphan products : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies
| Rare diseases and orphan products : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies |
| Edizione | [1st ed.] |
| Pubbl/distr/stampa | Washington, D.C. : , : National Academies Press, , 2010 |
| Descrizione fisica | 1 online resource (xxi, 420 pages) : illustrations |
| Disciplina | 615.19 |
| Altri autori (Persone) |
FieldMarilyn J (Marilyn Jane)
BoatThomas F |
| Soggetto topico |
Orphan drugs
Drugs - Design Rare diseases - Treatment |
| ISBN |
0-309-20991-9
1-283-04456-0 9786613044563 0-309-15807-9 |
| Formato | Materiale a stampa |
| Livello bibliografico | Monografia |
| Lingua di pubblicazione | eng |
| Nota di contenuto |
""Front Matter""; ""Acknowledgments""; ""Reviewers""; ""Preface""; ""Contents""; ""Boxes, Figures, and Tables""; ""Summary""; ""1 Introduction""; ""2 Profile of Rare Diseases""; ""3 Regulatory Framework for Drugs for Rare Diseases""; ""4 Discovery Research for Rare Diseases and Orphan Product Development""; ""5 Development of New Therapeutic Drugs and Biologics for Rare Diseases""; ""6 Coverage and Reimbursement: Incentives and Disincentives for Product Development""; ""7 Medical Devices: Research and Development for Rare Diseases""
""8 Toward an Integrated Approach to Accelerating Research and Product Development for Rare Diseases""; ""References""; ""Appendix A: Study Activities""; ""Appendix B: Innovation and the Orphan Drug Act, 1983-2009: Regulatory and Clinical Characteristics of Approved Orphan Drugs""; ""Appendix C: Medicare Part D Coverage and Reimbursement of Orphan Drugs""; ""Appendix D: Glossary, Abbreviations, and Public Laws""; ""Appendix E: Rare Diseases Clinical Research Network""; ""Appendix F: Advocacy Group Approaches to Accelerating Research and Product Development: Illustrative Examples""; ""Appendix G: Committee and Staff Biographies""; ""Index"" |
| Record Nr. | UNINA-9910825782703321 |
| Washington, D.C. : , : National Academies Press, , 2010 | ||
| Materiale a stampa | ||
| Lo trovi qui: Univ. Federico II | ||
| ||
