00455oas 2200181z- 450 99108471454033212399-5270(CKB)4100000012155756(EXLCZ)99410000001215575620230214cuuuuuuuu -u- -engFuture Rare DiseasesFuture Medicine Ltd2399-5262 JOURNAL9910847145403321Future Rare Diseases4154931UNINA