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Record Nr. |
UNINA9910825782703321 |
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Titolo |
Rare diseases and orphan products : accelerating research and development / / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies |
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Pubbl/distr/stampa |
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Washington, D.C. : , : National Academies Press, , 2010 |
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©2010 |
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ISBN |
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0-309-20991-9 |
1-283-04456-0 |
9786613044563 |
0-309-15807-9 |
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Edizione |
[1st ed.] |
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Descrizione fisica |
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1 online resource (xxi, 420 pages) : illustrations |
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Altri autori (Persone) |
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FieldMarilyn J (Marilyn Jane) |
BoatThomas F |
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Disciplina |
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Soggetti |
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Orphan drugs |
Drugs - Design |
Rare diseases - Treatment |
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Lingua di pubblicazione |
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Formato |
Materiale a stampa |
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Livello bibliografico |
Monografia |
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Note generali |
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Description based upon print version of record. |
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Nota di bibliografia |
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Includes bibliographical references (p. 249-282) and index. |
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Nota di contenuto |
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""Front Matter""; ""Acknowledgments""; ""Reviewers""; ""Preface""; ""Contents""; ""Boxes, Figures, and Tables""; ""Summary""; ""1 Introduction""; ""2 Profile of Rare Diseases""; ""3 Regulatory Framework for Drugs for Rare Diseases""; ""4 Discovery Research for Rare Diseases and Orphan Product Development""; ""5 Development of New Therapeutic Drugs and Biologics for Rare Diseases""; ""6 Coverage and Reimbursement: Incentives and Disincentives for Product Development""; ""7 Medical Devices: Research and Development for Rare Diseases"" |
""8 Toward an Integrated Approach to Accelerating Research and Product Development for Rare Diseases""; ""References""; ""Appendix A: Study Activities""; ""Appendix B: Innovation and the Orphan Drug Act, 1983-2009: Regulatory and Clinical Characteristics of Approved |
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